Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000669272 | SCV000794009 | likely pathogenic | Niemann-Pick disease, type A | 2017-09-06 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003767973 | SCV004574364 | pathogenic | Niemann-Pick disease, type B; Niemann-Pick disease, type A | 2023-09-04 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Trp32*) in the SMPD1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in SMPD1 are known to be pathogenic (PMID: 12369017, 15221801). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with Niemann-Pick disease (PMID: 32778503). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 553755). For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV000669272 | SCV005052845 | pathogenic | Niemann-Pick disease, type A | 2024-02-25 | criteria provided, single submitter | clinical testing |