Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001810403 | SCV002059986 | pathogenic | Monogenic diabetes | 2021-12-31 | reviewed by expert panel | curation | The c.1129delC variant in the HNF1 homeobox A gene, HNF1A, causes a frameshift in the protein at codon 377 (NM_000545.8), adding 7 novel amino acids before encountering a stop codon (p.(Leu377SerfsTer7)). This variant, located in biologically-relevant exon 6 of 10, is predicted to lead to nonsense mediated decay in a gene in which loss-of-function is an established disease mechanism (PVS1; PMID: 23348805). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). Also, this variant was identified in an individual with a clinical history highly specific for HNF1A-MODY (MODY probability calculator result >50%, negative genetic testing for HNF4A) (PP4; internal lab contributors). In summary, c.1129delC meets the criteria to be classified as pathogenic for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP VCEP (specification version 1.1, approved 6/4/2021): PVS1, PP4, PM2_Supporting |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000030476 | SCV000053146 | likely pathogenic | Maturity-onset diabetes of the young type 3 | 2011-08-18 | criteria provided, single submitter | curation | Converted during submission to Likely pathogenic. |
Invitae | RCV001852601 | SCV002203263 | pathogenic | not provided | 2020-12-10 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (ExAC no frequency). For these reasons, this variant has been classified as Pathogenic. This variant has been observed in individual(s) with maturity-onset diabetes of the young (PMID: 23348805). ClinVar contains an entry for this variant (Variation ID: 36796). This sequence change creates a premature translational stop signal (p.Leu377Serfs*7) in the HNF1A gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in HNF1A are known to be pathogenic (PMID: 15928245, 18003757). |
Clinical Genomics, |
RCV002326696 | SCV002601613 | likely pathogenic | Maturity onset diabetes mellitus in young | criteria provided, single submitter | research | Mutations in HNF1A gene can predispose to MODY3. It is associated with both micro and macrovascular complications of diabetes, especially cardiovascular complications. Associated with glucosuria. May respond well to sulfonylureas. However, more evidence is required to confer the association of this particular variant rs193922576 with MODY3. |