Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002260404 | SCV002540110 | pathogenic | Monogenic diabetes | 2022-06-10 | reviewed by expert panel | curation | The c.326+1G>T variant in the HNF1 homeobox A gene, HNF1A, is predicted to remove a canonical splice donor site in intron 1 of NM_000545.8. This variant is predicted to cause skipping of biologically-relevant exon 1 of 10, resulting in a frameshift, leading to nonsense mediated decay in a gene in which loss-of-function is an established disease mechanism (PVS1; PMID: 23348805). Additionally, this variant was identified in an individual with a clinical history highly specific for HNF1A-MODY (MODY probability calculator result >50%, negative genetic testing for HNF4A, and persistent positive C- peptide) (PP4_Moderate; internal lab contributors). The c.326+1G>A and c.326+1G>C variants at the same canonical nucleotide have been classified as pathogenic for monogenic diabetes by the ClinGen MDEP, and c.326+1G>T has a similar predicted impact on donor loss by Splice AI (0.98) (PS1_Supporting). Lastly, this variant is absent from gnomAD v2.1.1 (PM2_Supporting). In summary, c.326+1G>T meets the criteria to be classified as pathogenic for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP (specification version 1.1 approved 9/30/21): PVS1, PS1_Supporting, PP4_Moderate, PM2_Supporting. |
Genetic Services Laboratory, |
RCV001817891 | SCV002067322 | pathogenic | not provided | 2019-04-30 | criteria provided, single submitter | clinical testing |