Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV005401814 | SCV006059958 | uncertain significance | Monogenic diabetes | 2025-04-23 | reviewed by expert panel | curation | The c.340C>T variant in the HNF1 homeobox A gene, HNF1A, causes an amino acid change of arginine to cysteine at codon 114 (p.(Arg114Cys)) of NM_000545.8. This variant is located within a conserved region of the DNA binding domain (codons 107-174 and 201-280) of HNF1A, which is defined as critical for the protein’s function by the ClinGen MDEP (PM1_Supporting). This variant is predicted to be deleterious by computational evidence, with a REVEL score of 0.952, which is greater than the MDEP VCEP threshold of 0.70 (PP3). Functional studies demonstrated the p.Arg114Cys protein has DNA binding above 75% of wild type, normal localization, and transactivation above 75% of wildtype, indicating that this variant does not impact protein function (BS3_Supporting; PMID: 26853433). The Grpmax filtering allele frequency of the c.340C>T variant in gnomAD v2.1.1 is 0.00002596, which falls between ClinGen MDEP-established cutoffs for PM2_Supporting and BS1; thus, neither criterion will be applied. This variant was identified in four unrelated individuals with non-autoimmune and non-absolute/near-absolute insulin-deficient diabetes; however, PS4 cannot be applied because the variant MAF in gnomAD is above the ClinGen MDEP PM2_Supporting cutoff (PMIDs:26853433, 19336507, ClinVar, internal lab contributors). In summary, c.340C>T meets the criteria to be classified as variant of uncertain significance for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP (specification version 2.1.0, approved 8/11/2023): PM1_Supporting, PP3, BS3_Supporting. |
Broad Center for Mendelian Genomics, |
RCV001248949 | SCV001422728 | uncertain significance | Maturity-onset diabetes of the young type 3 | 2020-01-22 | criteria provided, single submitter | curation | The p.Arg114Cys variant in HNF1A has not been previously reported in individuals with maturity-onset diabetes of the young and has been identified in 0.01% (3/30610) of South Asian chromosomes by the Genome Aggregation Database (gnomAD, http://gnomad.broadinstitute.org; dbSNP rs774996577). Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. In summary, the clinical significance of the p.Arg114Cys variant is uncertain. ACMG/AMP Criteria applied: BS1, PP3 (Richards 2015). |
Molecular Genetics, |
RCV002051926 | SCV002318386 | uncertain significance | Maturity onset diabetes mellitus in young | criteria provided, single submitter | clinical testing | ||
Clinical Genomics, |
RCV002051926 | SCV002758781 | likely risk allele | Maturity onset diabetes mellitus in young | criteria provided, single submitter | research | Mutations in HNF1A gene can predispose to MODY3. It is associated with both micro and macrovascular complications of diabetes, especially cardiovascular complications. Associated with glucosuria. May respond well to sulfonylureas. However, more evidence is required to confer the association of this particular variant rs774996577 with MODY3. | |
Gene |
RCV004797916 | SCV005419917 | uncertain significance | not provided | 2024-05-23 | criteria provided, single submitter | clinical testing | Reported in an individual with suspected MODY in published literature (PMID: 19336507); detailed clinical and segregation information not provided; Published functional studies demonstrate impaired DNA binding but do not significantly impact transcription, expression, or nuclear localization (PMID: 26853433, 32910913); further studies are necessary to elucidate the role of the variant; Located in the critical DNA binding domain (PMID: 12453420, 18003757); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 26853433, 12453420, 18003757, 32910913, 23348805, 19336507) |
Fulgent Genetics, |
RCV005005125 | SCV005632351 | uncertain significance | Diabetes mellitus type 1; Type 1 diabetes mellitus 20; Maturity-onset diabetes of the young type 3; Type 2 diabetes mellitus; Hepatic adenomas, familial; Nonpapillary renal cell carcinoma | 2024-06-03 | criteria provided, single submitter | clinical testing | |
Neuberg Centre For Genomic Medicine, |
RCV001248949 | SCV006070574 | likely pathogenic | Maturity-onset diabetes of the young type 3 | 2024-02-01 | criteria provided, single submitter | clinical testing | Missense 0.001% Polyphen: possibly damaging SIFT: damaging MutationTaster: disease causing CADD Phred: damaging SpliceAI: NA GERP++ PhyloP Uncertain Significance/Likely risk allele Yes Radha V, et al., 2019; Balamurugan K, et al., 2016 |