Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Division of Genomic Medicine, |
RCV002274817 | SCV002559804 | likely pathogenic | Tuberous sclerosis 2 | 2022-07-19 | criteria provided, single submitter | clinical testing | According to ACMG GL 2015, this variant located in Hamartin binding domain (PM1), absent from controls (PM2), assumed de novo (PM6), multiple lines of computational evidence support a deleterious effect (PP3). |
Gene |
RCV004770435 | SCV005378762 | uncertain significance | not provided | 2023-12-14 | criteria provided, single submitter | clinical testing | Observed once in the mosaic state in a cohort of individuals with a clinical diagnosis or suspected tuberous sclerosis complex; however, the patient's phenotype and family history were not specified (PMID: 36232477); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 36232477) |