Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV004018210 | SCV004848772 | likely pathogenic | Hereditary von Willebrand disease | 2022-08-26 | criteria provided, single submitter | clinical testing | The c.2968-1G>A variant in VWF has not been reported in individuals with disease and was absent from large population studies. This variant occurs within the canonical splice site (+/- 1,2) and is predicted to cause altered splicing leading to an abnormal or absent protein. Loss of function of the VWF gene is associated with von Willebrand disease. In summary, although additional studies are required to fully establish its clinical significance, this variant meets criteria to be classified as likely pathogenic for autosomal dominant von Willebrand disease. ACMG/AMP criteria applied: PM2_supporting, PVS1. |