Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001071559 | SCV001236868 | pathogenic | Leber congenital amaurosis 7; Cone-rod dystrophy 2 | 2024-12-18 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with tryptophan, which is neutral and slightly polar, at codon 40 of the CRX protein (p.Arg40Trp). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with autosomal dominant cone-rod dystrophy (PMID: 26161267, 29785639, 31626798, 32533067). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 864383). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) indicates that this missense variant is expected to disrupt CRX protein function with a positive predictive value of 95%. For these reasons, this variant has been classified as Pathogenic. |
Blueprint Genetics | RCV001075179 | SCV001240791 | pathogenic | Retinal dystrophy | 2018-11-02 | criteria provided, single submitter | clinical testing | |
Institute of Medical Molecular Genetics, |
RCV001352999 | SCV001548091 | likely pathogenic | Cone-rod dystrophy 2 | 2021-01-30 | criteria provided, single submitter | clinical testing | |
3billion, |
RCV001352999 | SCV004013475 | likely pathogenic | Cone-rod dystrophy 2 | criteria provided, single submitter | clinical testing | The variant is observed at an extremely low frequency in the gnomAD v2.1.1 dataset (total allele frequency: <0.001%). In silico tool predictions suggest damaging effect of the variant on gene or gene product (REVEL: 0.94). Same nucleotide change resulting in same amino acid change has been previously reported as pathogenic/likely pathogenic with strong evidence (ClinVar ID: VCV000864383 / PMID: 26161267). A different missense change at the same codon (p.Arg40Gln) has been reported to be associated with CRX related disorder (ClinVar ID: VCV000437959 / PMID: 28041643). Therefore, this variant is classified as Likely pathogenic according to the recommendation of ACMG/AMP guideline. | |
Gene |
RCV003318660 | SCV004022736 | likely pathogenic | not provided | 2023-07-18 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 31626798, 29785639, 32566799, 32533067, 33546218, 35836572, 37239417, 36284460, 32112665, 26161267) |
Dept Of Ophthalmology, |
RCV001075179 | SCV004706289 | likely pathogenic | Retinal dystrophy | 2023-10-01 | criteria provided, single submitter | research |