Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Mendelics | RCV002249293 | SCV002518565 | pathogenic | Maple syrup urine disease | 2022-05-04 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV002249293 | SCV003443336 | likely pathogenic | Maple syrup urine disease | 2023-12-11 | criteria provided, single submitter | clinical testing | This sequence change replaces aspartic acid, which is acidic and polar, with asparagine, which is neutral and polar, at codon 152 of the BCKDHA protein (p.Asp152Asn). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with maple syrup urine disease (PMID: 18378174; Invitae). ClinVar contains an entry for this variant (Variation ID: 1685566). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt BCKDHA protein function with a positive predictive value of 95%. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
Fulgent Genetics, |
RCV005017161 | SCV005648297 | likely pathogenic | Maple syrup urine disease type 1A | 2024-02-15 | criteria provided, single submitter | clinical testing |