Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000004479 | SCV000797972 | pathogenic | Cholestanol storage disease | 2018-02-22 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000004479 | SCV001220276 | pathogenic | Cholestanol storage disease | 2024-01-25 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 4 of the CYP27A1 gene. RNA analysis indicates that disruption of this splice site induces altered splicing and likely results in a shortened protein product. This variant is present in population databases (rs397515354, gnomAD 0.002%). Disruption of this splice site has been observed in individual(s) with cerebrotendinous xanthomatosis (PMID: 8514861, 9254865, 10430841). It has also been observed to segregate with disease in related individuals. This variant is also known as 865+1G>A. ClinVar contains an entry for this variant (Variation ID: 4257). Studies have shown that disruption of this splice site results in skipping of exon 4, but is expected to preserve the integrity of the reading-frame (PMID: 9254865). For these reasons, this variant has been classified as Pathogenic. |
Institute of Medical Genetics and Applied Genomics, |
RCV001268682 | SCV001447795 | pathogenic | not provided | 2020-10-23 | criteria provided, single submitter | clinical testing | |
Gene |
RCV001268682 | SCV005201737 | pathogenic | not provided | 2023-09-18 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect (skipping of exon 4 and leading to a loss of 198bp in the mRNA and of 66 amino acids in the enzyme molecule) (PMID: 9254865); Not observed at significant frequency in large population cohorts (gnomAD); Also known as c.865+1G>A; This variant is associated with the following publications: (PMID: 25525159, 31589614, 20301583, 10430841, 27678445, 9254865) |
OMIM | RCV000004479 | SCV000024652 | pathogenic | Cholestanol storage disease | 1993-06-01 | no assertion criteria provided | literature only | |
Gene |
RCV000004479 | SCV000087232 | pathologic | Cholestanol storage disease | 2013-08-01 | no assertion criteria provided | curation | Converted during submission to Pathogenic. |
Natera, |
RCV000004479 | SCV002078785 | pathogenic | Cholestanol storage disease | 2017-09-26 | no assertion criteria provided | clinical testing |