Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000014076 | SCV005380588 | likely pathogenic | Pyruvate dehydrogenase E1-beta deficiency | 2024-08-19 | criteria provided, single submitter | clinical testing | Variant summary: PDHB c.395A>G (p.Tyr132Cys) results in a non-conservative amino acid change located in the Transketolase-like, pyrimidine-binding domain (IPR005475) of the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant was absent in 251494 control chromosomes. c.395A>G has been reported in the literature in individuals affected with Pyruvate Dehydrogenase E1-Beta Deficiency (examples:Brown_2004,Okajima_2008). These data indicate that the variant is likely to be associated with disease . At least one publication reports experimental evidence evaluating an impact on protein function. The most pronounced variant effect results in 16% of normal activity (Okajima_2008). The following publications have been ascertained in the context of this evaluation (PMID: 15138885, 18164639). ClinVar contains an entry for this variant (Variation ID: 13188). Based on the evidence outlined above, the variant was classified as likely pathogenic. |
OMIM | RCV000014076 | SCV000034323 | pathogenic | Pyruvate dehydrogenase E1-beta deficiency | 2004-07-01 | no assertion criteria provided | literature only |