Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV003441708 | SCV004170698 | pathogenic | not provided | 2023-10-31 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect with increased GTPase activity (PMID: 20700106); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 24077912, 20700106, 17932957, 25214167, 16227997) |
OMIM | RCV000007709 | SCV000027910 | pathogenic | Severe X-linked myotubular myopathy | 2007-12-01 | no assertion criteria provided | literature only | |
Inherited Neuropathy Consortium Ii, |
RCV003447079 | SCV004174710 | uncertain significance | Charcot-Marie-Tooth disease dominant intermediate B | 2016-01-06 | no assertion criteria provided | literature only |