Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Johns Hopkins Genomics, |
RCV003150899 | SCV003839105 | likely pathogenic | Polycystic kidney disease, adult type | 2022-12-23 | criteria provided, single submitter | clinical testing | This PKD1 variant is absent in a large population dataset and has not been reported in ClinVar, nor the literature in association with ADPKD to our knowledge. This frameshift variant in exon 12 of 46 results in a premature termination codon (PTC) likely leading to nonsense-mediated decay and lack of protein production. We consider c.2865dupC (p.Val956fs) to be likely pathogenic. |