Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetics and Molecular Pathology, |
RCV002272738 | SCV002556862 | pathogenic | Spinocerebellar ataxia 47 | 2020-09-07 | criteria provided, single submitter | clinical testing | A de novo novel heterozygous frameshift variant was detected in the PUM1 gene. Pathogenic PUM1 mutations have been associated with neurodevelopmental disorders and seizures (PMID: 31859446; PMID: 29474920). Alternate transcript isoforms have been described for PUM1; this variant is in exon 2 of transcript NM_001020658.1 and expressed in multiple tissues. |