Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV002375652 | SCV002624446 | pathogenic | Diamond-Blackfan anemia | 2016-08-04 | criteria provided, single submitter | clinical testing | The p.M1? pathogenic mutation (also known as c.3G>C) is located in coding exon 1 of the RPS19 gene and results from a G to C substitution at nucleotide position 3. This alters the methionine residue at the initiation codon. This mutation was reported as a de novo occurrence in a patient with a clinical diagnosis of Diamond-Blackfan Anemia. The same study also described another affected individual with a mutation at the same codon (Ramenghi U et al. Blood Cells Mol. Dis., 2000 Oct;26:417-22). In addition to the clinical data presented in the literature, since sequence variations that modify the initiation codon (ATG) are expected to result in either loss of translation initiation, N-terminal truncation, or cause a shift in the mRNA reading frame, this alteration is interpreted as a disease-causing mutation. |