Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000187013 | SCV000240586 | pathogenic | not provided | 2014-04-18 | criteria provided, single submitter | clinical testing | p.Gln317Stop (CAG>TAG): c.949 C>T in exon 13 of the CLN3 gene (NM_001042432.1) The Q317X nonsense mutation in the CLN3 gene is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. Although this mutation has not been reported previously to our knowledge, it is considered a disease-causing mutation. The variant is found in EPILEPSY panel(s). |
Genome- |
RCV001729442 | SCV001977442 | pathogenic | Neuronal ceroid lipofuscinosis 3 | 2021-08-10 | criteria provided, single submitter | clinical testing | |
Victorian Clinical Genetics Services, |
RCV001729442 | SCV002557849 | pathogenic | Neuronal ceroid lipofuscinosis 3 | 2022-02-02 | criteria provided, single submitter | clinical testing | Based on the classification scheme VCGS_Germline_v1.3.4, this variant is classified as Pathogenic. Following criteria are met: 0102 - Loss of function is a known mechanism of disease in this gene and is associated with neuronal ceroid lipofuscinosis, 3 (MIM#204200) and nonsyndromic retinal degeneration (PMID: 31568712). (I) 0106 - This gene is associated with autosomal recessive disease. (I) 0201 - Variant is predicted to cause nonsense-mediated decay (NMD) and loss of protein (premature termination codon is located at least 54 nucleotides upstream of the final exon-exon junction). (SP) 0252 - This variant is homozygous. (I) 0304 - Variant is present in gnomAD <0.01 for a recessive condition (v3: 1 heterozygote, 0 homozygotes). (SP) 0701 - Other NMD-predicted variants comparable to the one identified in this case have very strong previous evidence for pathogenicity. There are multiple likely pathogenic and pathogenic NMD-predicted variants that have been described (ClinVar, PMID: 31568712). (SP) 0803 - This variant has limited previous evidence of pathogenicity in an unrelated individual. This variant has been classified once as pathogenic by a clinical diagnostic laboratory (ClinVar). (SP) 0905 - No published segregation evidence has been identified for this variant. (I) 1007 - No published functional evidence has been identified for this variant. (I) 1208 - Inheritance information for this variant is not currently available in this individual. (I) Legend: (SP) - Supporting pathogenic, (I) - Information, (SB) - Supporting benign |
Labcorp Genetics |
RCV002516983 | SCV003312475 | pathogenic | Neuronal ceroid lipofuscinosis | 2023-02-20 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 205092). This variant has not been reported in the literature in individuals affected with CLN3-related conditions. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Gln317*) in the CLN3 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CLN3 are known to be pathogenic (PMID: 9311735, 28542676). |
Fulgent Genetics, |
RCV001729442 | SCV005646531 | likely pathogenic | Neuronal ceroid lipofuscinosis 3 | 2024-04-01 | criteria provided, single submitter | clinical testing |