Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics, |
RCV001800164 | SCV002041906 | pathogenic | Neurofibromatosis, type 1 | 2021-12-27 | criteria provided, single submitter | clinical testing | The variant c.6756+1G>T (p.?) is located in the donor splice site of intron 44 of the NF1-gene, it affects a canonical splice site and it is not found in the gnomAD database. In silico programs predict a significant impact on NF1-RNA splicing (varSEAK SSP, SpliceSiteFinder-like, MaxEntScan, NNSPLICE and GeneSplicer), which has not been validated by functional studies yet. This variant has already been identified in an individual with Neurofibromatosis, type 1 (PMID: 31766501). ACMG criteria used for classification: PVS1, PM2, PP5. |
3billion | RCV002283558 | SCV002573181 | pathogenic | Neurofibromatosis-Noonan syndrome | 2022-09-01 | criteria provided, single submitter | clinical testing | The variant is not observed in the gnomAD v2.1.1 dataset. Canonical splice site is predicted to alter splicing and result in a loss or disruption of normal protein function. Multiple pathogenic loss-of-function variants are reported downstream of the variant. The variant has been reported to be associated with NF1--related disorder (ClinVar ID: VCV001329856). Therefore, this variant is classified as Pathogenic according to the recommendation of ACMG/AMP guideline. |
Labcorp Genetics |
RCV001800164 | SCV004632647 | pathogenic | Neurofibromatosis, type 1 | 2023-11-08 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 44 of the NF1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in NF1 are known to be pathogenic (PMID: 10712197, 23913538). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individual(s) with neurofibromatosis type 1 (PMID: 10712197, 31766501). ClinVar contains an entry for this variant (Variation ID: 1329856). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV004720941 | SCV005328151 | pathogenic | not provided | 2023-05-24 | criteria provided, single submitter | clinical testing | Canonical splice site variant predicted to result in a null allele in a gene for which loss of function is a known mechanism of disease; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 31766501) |