Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Bertuch Lab, |
RCV001523791 | SCV001450737 | pathogenic | Dyskeratosis congenita, autosomal dominant 6 | criteria provided, single submitter | clinical testing | This variant consists of deletion of a single nucleotide in exon 4, resulting in frameshift and production of a premature termination codon in exon 5. When heterozygous, this variant, which was studied in a father and son, produced no clinical phenotype. Telomere length by flow-FISH analysis in the two individuals revealed lymphocyte telomere lengths that were within normal range. When compound heterozygous with an in-frame deletion of amino acid E169, this variant resulted in extremely short telomeres and severe clinical phenotypes. |