Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Broad Center for Mendelian Genomics, |
RCV001267703 | SCV001445954 | likely pathogenic | Congenital myopathy with fiber type disproportion | 2020-11-16 | criteria provided, single submitter | curation | The heterozygous p.Ile194_Glu197delinsLys variant in ACTA1 was identified by our study in 1 individual with congenital fiber-type disproportion myopathy. Trio genome analysis showed this variant to be de novo. The variant has not been previously reported in individuals with congenital fiber-type disproportion myopathy and was absent from large population studies. This variant is a deletion of 9 bases at position 581 and is not predicted to alter the protein reading-frame. It is unclear if this deletion will impact the protein. In summary, although additional studies are required to fully establish its clinical significance, this variant is likely pathogenic. ACMG/AMP Criteria applied: PS2, PM2, PM4 (Richards 2015). |