Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics Munich, |
RCV000995477 | SCV001149663 | pathogenic | Congenital myopathy with fiber type disproportion | 2017-10-27 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001869389 | SCV002110120 | pathogenic | Actin accumulation myopathy | 2022-06-27 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 807361). This premature translational stop signal has been observed in individual(s) with autosomal recessive ACTA1-related conditions (PMID: 29172004). This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Glu228*) in the ACTA1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in ACTA1 are known to be pathogenic (PMID: 19562689). |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV004587005 | SCV005076750 | pathogenic | Congenital myopathy 2c, severe infantile, autosomal dominant | 2024-04-10 | criteria provided, single submitter | clinical testing | Variant summary: ACTA1 c.682G>T (p.Glu228X) results in a premature termination codon, predicted to cause absence of the protein due to nonsense mediated decay, which is a commonly known mechanism for ACTA1-related AR alpha-actinopathy. The variant was absent in 250632 control chromosomes. c.682G>T has been reported in the literature in at-least one individual from a cohort of Early-Onset Myopathies, however detailed information was not available (Vill_2017). To our knowledge, no experimental evidence demonstrating an impact on protein function has been reported. The following publication have been ascertained in the context of this evaluation (PMID: 29172004). ClinVar contains an entry for this variant (Variation ID: 807361). Based on the evidence outlined above, the variant was classified as pathogenic. |