Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV002293418 | SCV002586691 | pathogenic | not provided | 2024-07-10 | criteria provided, single submitter | clinical testing | Identified in multiple patients with features of ACTB-related Baraitser-Winter syndrome in published literature and tested at GeneDx, reported de novo with or without confirmed parentage when parental samples were available (PMID: 38444904, 25052316); Missense variants in this gene are a common cause of disease and they are underrepresented in the general population; In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 22366783, 38444904, 25052316) |
Foundation for Research in Genetics and Endocrinology, |
RCV000133564 | SCV004565366 | likely pathogenic | Baraitser-Winter syndrome 1 | 2024-02-12 | criteria provided, single submitter | clinical testing | A heterozygous missense variant in exon 3 of the ACTB gene that results in the amino acid substitution of Phenylalanine for Leucine at codon 65 (p.Leu65Phe) was detected. The observed variant and a different missense in the same codon (p.Leu65Val) has previously been reported in patients affected with Baraitser-Winter syndrome [PMID: 25052316, ClinVar: VCV000127161.4]. This variant has not been reported in the 1000 genomes, gnomAD (v3.1), gnomdAD (v2.1) and topmed databases. The in silico prediction of the variant are probably damaging by PolyPhen-2 (HumDiv), SIFT and LRT. The reference codon is conserved across species. In summary, the variant meets our criteria to be classified as a likely pathogenic. |
Department of Genetics, |
RCV000133564 | SCV000148634 | pathogenic | Baraitser-Winter syndrome 1 | 2014-04-15 | no assertion criteria provided | clinical testing | |
Diagnostic Laboratory, |
RCV001249485 | SCV001423475 | pathogenic | Intellectual disability | 2018-12-01 | no assertion criteria provided | clinical testing |