Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002233679 | SCV000828569 | uncertain significance | Heterotopia, periventricular, X-linked dominant; Melnick-Needles syndrome; Oto-palato-digital syndrome, type II; Frontometaphyseal dysplasia | 2023-07-29 | criteria provided, single submitter | clinical testing | This sequence change replaces phenylalanine, which is neutral and non-polar, with serine, which is neutral and polar, at codon 2251 of the FLNA protein (p.Phe2251Ser). This variant is present in population databases (no rsID available, gnomAD 0.001%). This variant has not been reported in the literature in individuals affected with FLNA-related conditions. ClinVar contains an entry for this variant (Variation ID: 577159). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on FLNA protein function. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
NIHR Bioresource Rare Diseases, |
RCV000851611 | SCV000899363 | uncertain significance | Macrothrombocytopenia | 2019-02-01 | criteria provided, single submitter | research | |
Prevention |
RCV004535741 | SCV004113296 | uncertain significance | FLNA-related disorder | 2023-02-06 | criteria provided, single submitter | clinical testing | The FLNA c.6776T>C variant is predicted to result in the amino acid substitution p.Phe2259Ser. This variant has been reported in the hemizygous state in two individuals with platelet count disorders (Table S3 - Downes et al. 2019. PubMed ID: 31064749). This variant is reported in 0.0012% of alleles in individuals of European (Non-Finnish) descent in gnomAD (http://gnomad.broadinstitute.org/variant/X-153580383-A-G). At this time, the clinical significance of this variant is uncertain due to the absence of conclusive functional and genetic evidence. |