Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Centre for Population Genomics, |
RCV000170198 | SCV004809012 | pathogenic | Rett syndrome | 2024-03-14 | criteria provided, single submitter | curation | This variant has been collected from RettBASE and curated to current modified ACMG/AMP criteria. Based on the classification scheme defined by the ClinGen Rett/Angelman-like Expert Panel for Rett/AS-like Disorders Specifications to the ACMG/AMP Variant Interpretation Guidelines VCEP 3.0, this variant is classified as pathogenic. At least the following criteria are met: Predicted to result in loss of function, and LOF is a known mechanism of disease (PVS1). This variant has been identified as a de novo occurrence in an individual with Rett syndrome with confirmed parental relationships (PS2) PMID: 11309679 This variant is absent from gnomAD (PM2_Supporting). Has been observed in at least 2 individuals with phenotypes consistent with MECP2-related disease (PS4_Supporting). PMID: 11309679, PMID: 27267200 |
Rett |
RCV000144112 | SCV000189188 | not provided | not provided | flagged submission | not provided | ||
Rett |
RCV000170198 | SCV000222527 | pathogenic | Rett syndrome | 2003-03-31 | no assertion criteria provided | curation | |
Prevention |
RCV004532624 | SCV004748235 | pathogenic | MECP2-related disorder | 2023-12-08 | no assertion criteria provided | clinical testing | The MECP2 c.378-2A>C variant is predicted to disrupt the AG splice acceptor site and interfere with normal splicing. This variant was reported in an individual with Rett syndrome and mRNA analysis further confirmed a deletion caused by abnormal splicing (Bourdon et al 2001. PubMed ID: 11214906). Of note, other splicing variants affecting the same nucleotide (c.378-2A>G, c.378-2A.T) have also been reported to be causative for Rett syndrome (HGMD database, Wen et al. 2020. PubMed ID: 32472557). This variant has not been reported in a large population database (http://gnomad.broadinstitute.org), indicating this variant is rare. Variants that disrupt the consensus splice acceptor site in MECP2 are expected to be pathogenic. This variant is interpreted as pathogenic. |