Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000544536 | SCV000656706 | pathogenic | Episodic ataxia type 2; Developmental and epileptic encephalopathy, 42 | 2017-07-19 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Donor and acceptor splice site variants typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in CACNA1A are known to be pathogenic (PMID: 10371528, 19486177, 25735478, 27250579). This variant has been reported to segregate with in a family with clinical features of CACNA1A-related disease (Invitae). This variant is not present in population databases (ExAC no frequency). This sequence change affects a donor splice site in intron 7 of the CACNA1A gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. |