Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV004606147 | SCV005099560 | pathogenic | Inborn genetic diseases | 2024-03-22 | criteria provided, single submitter | clinical testing | The c.4068delC (p.I1357Sfs*15) alteration, located in exon 25 (coding exon 25) of the CACNA1A gene, consists of a deletion of one nucleotide at position 4068, causing a translational frameshift with a predicted alternate stop codon after 15 amino acids. This alteration is expected to result in loss of function by premature protein truncation or nonsense-mediated mRNA decay. for episodic ataxia, type 2; however, its clinical significance for CACNA1A-related neurologic disorder is uncertain, and it is unlikely to be causative of CACNA1A-related spinocerebellar ataxia. This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). Based on the available evidence, this alteration is classified as pathogenic. |