Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003574698 | SCV004292555 | pathogenic | Qualitative or quantitative defects of dysferlin | 2023-05-13 | criteria provided, single submitter | clinical testing | This sequence change affects an acceptor splice site in intron 13 of the DYSF gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in DYSF are known to be pathogenic (PMID: 17698709, 20301480). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individual(s) with DYSF-related conditions (PMID: 18306167, 19528035). ClinVar contains an entry for this variant (Variation ID: 6683). Studies have shown that disruption of this splice site alters mRNA splicing and is expected to lead to the loss of protein expression (PMID: 25312915). For these reasons, this variant has been classified as Pathogenic. |
Laboratory of Medical Genetics, |
RCV000007070 | SCV005051754 | likely pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2B | 2024-02-01 | criteria provided, single submitter | curation | |
OMIM | RCV000007070 | SCV000027266 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2B | 2008-03-01 | no assertion criteria provided | literature only |