Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Medicine for Neurodegenerative and Neuromuscular Diseases Unit, |
RCV001647184 | SCV001519283 | pathogenic | Spastic ataxia | 2021-07-12 | criteria provided, single submitter | research | |
Gene |
RCV004762091 | SCV005373292 | uncertain significance | not provided | 2024-04-04 | criteria provided, single submitter | clinical testing | Observed as heterozygous variant in patient with ataxia in published literature; however, variants in other genes were also identified (PMID: 34445196); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 34445196) |