Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Rady Children's Institute for Genomic Medicine, |
RCV002279857 | SCV004046198 | pathogenic | Lymphatic malformation 12 | criteria provided, single submitter | clinical testing | This variant results in a c.391dup (p.Met131) change in an alternate MDFIC transcript NM_001166345.1. This frameshifting variant in exon 4 of 5 introduces a premature stop codon and is therefore predicted to result in loss of normal protein function through either protein truncation or nonsense-mediated mRNA decay (NMD). This variant has been previously reported as a homozygous and compound heterozygous change in patients with Central conducting lymphatic anomaly (PMID: 35235341). Functional studies confirm this variant results in a truncated protein (PMID: 35235341). The c.718dup (p.Met240AsnfsTer3) variant is present in the heterozygous state in the gnomAD population database at a frequency of 0.01770% (50/282438) and thus is presumed to be rare. Based on the available evidence, the c.718dup (p.Met240AsnfsTer3) variant is classified as Pathogenic. | |
Institute of Human Genetics, |
RCV002279857 | SCV005331506 | pathogenic | Lymphatic malformation 12 | 2024-09-20 | criteria provided, single submitter | clinical testing | |
OMIM | RCV002279857 | SCV002567898 | pathogenic | Lymphatic malformation 12 | 2022-08-23 | no assertion criteria provided | literature only | |
Prevention |
RCV003418436 | SCV004116381 | likely pathogenic | MDFIC-related disorder | 2024-08-19 | no assertion criteria provided | clinical testing | The MDFIC c.718dupA variant is predicted to result in a frameshift and premature protein termination (p.Met240Asnfs*3). Using an alternate transcript (NM_001166345), this variant is also referred to as c.391dupA (p.Met131Asnfs*3) in the literature. This variant has been reported in the homozygous and compound heterozygous states in multiple individuals with central conducting lymphatic anomaly with lymphedema (Byrne et al. 2022. PubMed ID: 35235341). Functional studies reveal that this variant escapes nonsense mediated decay, resulting in a truncated protein (Byrne et al. 2022. PubMed ID: 35235341). This variant is reported in 0.026% of alleles in individuals of European (non-Finnish) descent in gnomAD. This variant is interpreted as likely pathogenic. |