Total submissions: 8
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV000006950 | SCV000271307 | pathogenic | Autosomal recessive inherited pseudoxanthoma elasticum | 2015-03-11 | criteria provided, single submitter | clinical testing | The p.Arg1164X variant in ABCC6 has been previously reported in the homozygous s tate in one family with Pseudoxanthoma Elasticum (PXE; Struk 2000) and in 2 hete rozygous individuals with PXE in which another variant was not identified (Melon i 2001, Chassaing 2004). This variant has also been identified in 0.05% (4/8652 ) East Asian chromosomes by the Exome Aggregation Consortium (http://exac.broadi nstitute.org/; dbSNP rs72653744). Although this variant has been seen in the gen eral population, its frequency is low enough to be consistent with a recessive c arrier frequency. This nonsense variant leads to a premature termination codon a t position 1164, which is predicted to lead to a truncated or absent protein. Co mplete loss of ABCC6 function is an established disease mechanism for PXE. In su mmary, this variant meets our criteria to be classified as pathogenic for PXE in an autosomal recessive manner (www.partners.org/personalizedmedicine/lmm). |
Gene |
RCV000255402 | SCV000321367 | pathogenic | not provided | 2023-05-09 | criteria provided, single submitter | clinical testing | Reported in the heterozygous state in three patients with pseudoxanthoma elasticum from two families, although a second ABCC6 variant was not identified in these cases (Meloni et al., 2001; Chassaing et al., 2004); Nonsense variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss-of-function is a known mechanism of disease; This variant is associated with the following publications: (PMID: 1179012, 25525159, 28696355, 34205333, 34906475, 33879512, 31980526, 17617515, 11179012, 30056620, 29948180, 31269855, 30879837, 15086542, 28186352, 11439001, 10954200, 29480367, 31589614, 31345219) |
Fulgent Genetics, |
RCV001536083 | SCV001752784 | pathogenic | Autosomal recessive inherited pseudoxanthoma elasticum; Pseudoxanthoma elasticum, forme fruste; Arterial calcification, generalized, of infancy, 2 | 2021-06-30 | criteria provided, single submitter | clinical testing | |
Revvity Omics, |
RCV000255402 | SCV002018595 | pathogenic | not provided | 2023-12-29 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000255402 | SCV002137652 | pathogenic | not provided | 2024-01-29 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg1164*) in the ABCC6 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in ABCC6 are known to be pathogenic (PMID: 11536079, 17617515). This variant is present in population databases (rs72653744, gnomAD 0.07%). This premature translational stop signal has been observed in individuals with pseudoxanthoma elasticum (PMID: 11179012, 11439001). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 6572). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Laboratorio de Genetica e Diagnostico Molecular, |
RCV002251887 | SCV002523995 | pathogenic | See cases | 2021-09-03 | criteria provided, single submitter | clinical testing | ACMG classification criteria: PVS1, PS4, PM2, PM3 |
OMIM | RCV000006950 | SCV000027146 | pathogenic | Autosomal recessive inherited pseudoxanthoma elasticum | 2001-03-01 | no assertion criteria provided | literature only | |
PXE International | RCV000006950 | SCV000589062 | pathogenic | Autosomal recessive inherited pseudoxanthoma elasticum | 2021-03-01 | no assertion criteria provided | research |