Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Pediatric Nephrology Laboratory, |
RCV001027514 | SCV001190014 | pathogenic | Nail-patella syndrome | 2020-03-16 | criteria provided, single submitter | clinical testing | |
Pittsburgh Clinical Genomics Laboratory, |
RCV001027514 | SCV005397447 | pathogenic | Nail-patella syndrome | 2023-05-08 | criteria provided, single submitter | clinical testing | This sequence variant is a single nucleotide substitution (G>A) one base past the end of exon 5 of 8 of the LMX1B gene. This variant is predicted to disrupt the canonical donor splice of exon 5 resulting in the in-frame deletion of exon 5. This deletion would occur in the homeodomain of the LMX1B encoded protein, LIM homeobox transcription factor 1 beta. This is a previously reported variant (ClinVar) that has been observed in individuals affected by il-patella syndrome (PMID: 32457516, 28335748, 18535845). This variant is absent from the gnomAD population database (0 of approximately 250,000 alleles). To our knowledge, studies examining the functiol consequence of this variant have not been published. Based on the available evidence, we consider this a pathogenic variant. ACMG Criteria: PM2, PS4, PVS1 |