Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002007248 | SCV002236921 | pathogenic | Pyridoxine-dependent epilepsy | 2022-02-06 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln281*) in the ALDH7A1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in ALDH7A1 are known to be pathogenic (PMID: 16491085, 20554659). This variant is present in population databases (no rsID available, gnomAD 0.003%). For these reasons, this variant has been classified as Pathogenic. This variant is also known as p.Gln253Term. This premature translational stop signal has been observed in individual(s) with ALDH7A1-related conditions (PMID: 23350806). |