Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001858633 | SCV002232686 | pathogenic | not provided | 2023-09-14 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 801335). This variant is also known as p.Arg138*. This premature translational stop signal has been observed in individual(s) with spinal muscular atrophy with congenital bone fractures (PMID: 30327447). It has also been observed to segregate with disease in related individuals. This variant is present in population databases (no rsID available, gnomAD 0.009%). This sequence change creates a premature translational stop signal (p.Arg110*) in the ASCC1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in ASCC1 are known to be pathogenic (PMID: 30327447). |
Muscle and Diseases Team, |
RCV004586997 | SCV005038494 | pathogenic | Centronuclear myopathy | 2024-03-01 | criteria provided, single submitter | research | PVS1+PM2+PM4+PP3+PP5 |
Neuberg Centre For Genomic Medicine, |
RCV000986102 | SCV005400777 | pathogenic | Spinal muscular atrophy with congenital bone fractures 2 | 2023-06-22 | criteria provided, single submitter | clinical testing | The observed stop gain c.328C>T(p.Arg110Ter) variant in ASCC1 has been reported in homozygous state in individuals affected with ASCC1 related disorder (Rosano KK, et. al., 2021). It has also been observed to segregate with disease in related individuals (Böhm J, et. al., 2019). This variant is present with an allele frequency of 0.002% in gnomAD Exomes database. This variant has been reported to the ClinVar database as Pathogenic. Computational evidence (MutationTaster - disease causing) predict damaging effect on protein structure and function for this variant. The nucleotide change c.328C>T in ASCC1 is predicted as conserved by GERP++ and PhyloP across 100 vertebrates. This variant is predicted to cause loss of normal protein function through protein truncation. Loss of function variants have been previously reported to be disease causing (Böhm J, et. al., 2019). For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV001858633 | SCV005401452 | pathogenic | not provided | 2024-05-15 | criteria provided, single submitter | clinical testing | Nonsense variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss of function is a known mechanism of disease; This variant is associated with the following publications: (PMID: 34302381, 30327447) |
OMIM | RCV000986102 | SCV001134940 | pathogenic | Spinal muscular atrophy with congenital bone fractures 2 | 2020-01-03 | no assertion criteria provided | literature only |