Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Lupski Lab, |
RCV000076917 | SCV000266463 | pathogenic | DOORS syndrome | 2014-01-01 | criteria provided, single submitter | research | We identified 26 families with DOORS syndrome; each patient had at least 3 of the 5 well-described features of DOORS syndrome, which include deafness, onychodystrophy, osteodystrophy, intellectual disability, and seizures. A combination of whole-exome sequencing and Sanger sequencing identified homozygous or compound heterozygous pathogenic variants in TBC1D24 in 11 individuals from 9 families. |
OMIM | RCV000076917 | SCV000108714 | pathogenic | DOORS syndrome | 2014-01-01 | no assertion criteria provided | literature only |