Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Baylor Genetics | RCV000240839 | SCV000258398 | pathogenic | Progressive familial intrahepatic cholestasis type 1 | 2015-12-17 | criteria provided, single submitter | clinical testing | This variant was found in compound heterozygous status with another exonic deletion in two affected members of a Caucasian family |
OMIM | RCV000239480 | SCV000297937 | pathogenic | Cholestasis, progressive familial intrahepatic, 5 | 2016-07-27 | no assertion criteria provided | literature only | |
Prevention |
RCV004754355 | SCV005341232 | uncertain significance | NR1H4-related disorder | 2024-08-26 | no assertion criteria provided | clinical testing | The NR1H4 c.419_420insAAA variant is predicted to result in an in-frame amino acid insertion (p.Tyr139_Asn140insLys). This variant was reported in the compound heterozygous state with another exonic deletion in two related individuals with familial intrahepatic cholestasis (Gomez-Ospina et al 2016. PubMed ID: 26888176). This variant is reported in 0.00088% of alleles in individuals of European (Non-Finnish) descent in gnomAD. This variant has interpretations of pathogenic in ClinVar (https://www.ncbi.nlm.nih.gov/clinvar/variation/219162/). Although we suspect that this variant may be pathogenic, at this time, the clinical significance of this variant is uncertain due to the absence of conclusive functional and genetic evidence. |