Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001065092 | SCV001230031 | pathogenic | Congenital myasthenic syndrome 12 | 2022-11-14 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg322*) in the GFPT1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in GFPT1 are known to be pathogenic (PMID: 23794683). For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 859066). This variant is also known as c.910C>T (p.Arg304X). This premature translational stop signal has been observed in individual(s) with congenital myasthenic syndrome (PMID: 23794683). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. This variant is present in population databases (rs375268742, gnomAD 0.007%). |