Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Neuberg Centre For Genomic Medicine, |
RCV003337916 | SCV004048342 | likely pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2J | criteria provided, single submitter | clinical testing | The frameshift variant c.100881_100882del (p.Glu33627AspfsTer30) in TTN gene has not been reported previously as a pathogenic variant nor as a benign variant, to our knowledge. The p.Glu33627AspfsTer30 variant is novel (not in any individuals) in 1000 Genomes and is present in the gnomAD exomes database with a frequency of 0.0004%. Null variant (frame-shift), in gene TTN for which loss-of-function is a known mechanism of disease. This variant causes a frameshift starting with codon Glutamic Acid 33627, changes this amino acid to Aspartic Acid residue, and creates a premature Stop codon at position 30 of the new reading frame, denoted p.Glu33627AspfsTer30. For these reasons, this variant has been classified as Likely Pathogenic |