Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Broad Center for Mendelian Genomics, |
RCV001005016 | SCV001164578 | uncertain significance | X-linked sideroblastic anemia with ataxia | 2023-05-02 | criteria provided, single submitter | curation | The hemizygous c.1939-3C>G variant in ABCB7 was identified by our study in one individual with sideroblastic anemia. The c.1939-3C>G variant in ABCB7 has not been previously reported in individuals with X-linked sideroblastic anemia with ataxia. This variant was absent from large population studies. This variant has also been reported in Clinvar (Variation ID: 814010) and has been interpreted as a variant of uncertain significance by the Broad Institute Rare Disease Group. This variant is located in the 3' splice region. Computational tools do suggest an impact to splicing. However, this information is not predictive enough to determine pathogenicity. In summary, the clinical significance of the c.406+4A>G variant is uncertain. ACMG/AMP Criteria applied: PM2_Supporting, PP3 (Richards 2015). |