Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Kasturba Medical College, |
RCV001095802 | SCV002053904 | likely pathogenic | Liberfarb syndrome | criteria provided, single submitter | clinical testing | ||
Neuberg Centre For Genomic Medicine, |
RCV001095802 | SCV002072899 | pathogenic | Liberfarb syndrome | criteria provided, single submitter | clinical testing | The missense variant p.C300Y in PISD (NM_001326411.1) has been previously reported in affected patients and C266Y (Girisha KM et al; Zhao T et al).Functional analysis revealed a damaging effect. The p.C300Y variant is novel (not in any individuals) in gnomAD Exomes and is novel (not in any individuals) in 1000 Genomes. The p.C300Y missense variant is predicted to be damaging by both SIFT and PolyPhen2. The cysteine residue at codon 300 of PISD is conserved in all mammalian species. The nucleotide c.899 in PISD is predicted conserved by GERP++ and PhyloP across 100 vertebrates. For these reasons, this variant has been classified as Pathogenic. | |
OMIM | RCV001095802 | SCV001251646 | pathogenic | Liberfarb syndrome | 2020-05-20 | no assertion criteria provided | literature only |