Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000668128 | SCV000792679 | uncertain significance | Smith-Lemli-Opitz syndrome | 2017-07-07 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000668128 | SCV004294114 | likely pathogenic | Smith-Lemli-Opitz syndrome | 2022-11-01 | criteria provided, single submitter | clinical testing | In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. This variant disrupts the p.Arg404 amino acid residue in DHCR7. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 9653161, 10677299, 12818773, 15896653). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt DHCR7 protein function. ClinVar contains an entry for this variant (Variation ID: 552797). This missense change has been observed in individual(s) with clinical features of DHCR7-related conditions (PMID: 10677299, 10814720, 33578785). This variant is present in population databases (no rsID available, gnomAD 0.0009%). This sequence change replaces arginine, which is basic and polar, with serine, which is neutral and polar, at codon 404 of the DHCR7 protein (p.Arg404Ser). |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000668128 | SCV005205268 | likely pathogenic | Smith-Lemli-Opitz syndrome | 2024-06-05 | criteria provided, single submitter | clinical testing | Variant summary: DHCR7 c.1210C>A (p.Arg404Ser) results in a non-conservative amino acid change in the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 4.1e-06 in 241396 control chromosomes. c.1210C>A has been reported in the literature in individuals affected with Smith-Lemli-Opitz Syndrome (e.g. Witsch-Baumgartner_2000, Yu_2000, Zaidi_2021). These data indicate that the variant may be associated with disease. A different variant affecting the same codon has been classified as pathogenic by our lab (c.1210C>T, p.Arg404Cys), supporting the critical relevance of codon 404 to DHCR7 protein function. To our knowledge, no experimental evidence demonstrating an impact on protein function has been reported. ClinVar contains an entry for this variant (Variation ID: 552797). Based on the evidence outlined above, the variant was classified as likely pathogenic. |
Fulgent Genetics, |
RCV000668128 | SCV005630294 | likely pathogenic | Smith-Lemli-Opitz syndrome | 2024-06-06 | criteria provided, single submitter | clinical testing |