Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory of Molecular Genetics |
RCV000782013 | SCV000920475 | likely pathogenic | not provided | 2017-11-22 | criteria provided, single submitter | clinical testing | |
Ce |
RCV000782013 | SCV001247854 | pathogenic | not provided | 2023-09-01 | criteria provided, single submitter | clinical testing | SHANK3: PVS1:Strong, PM2, PS2:Moderate, PS4:Moderate |
Gene |
RCV000782013 | SCV001776415 | pathogenic | not provided | 2021-10-27 | criteria provided, single submitter | clinical testing | Frameshift variant predicted to result in protein truncation as the last 180 amino acids are replaced with 13 different amino acids, and other loss-of-function variants have been reported downstream in the Human Gene Mutation Database (Stenson et al., 2014); Not observed at significant frequency in large population cohorts (Lek et al., 2016); This variant is associated with the following publications: (PMID: 32050889) |
Ambry Genetics | RCV004027330 | SCV004946656 | pathogenic | Inborn genetic diseases | 2024-01-02 | criteria provided, single submitter | clinical testing | The c.4649_4653dupGCAGC (p.P1552Afs*14) alteration, located in exon 22 (coding exon 22) of the SHANK3 gene, consists of a duplication of GCAGC at position 4649, causing a translational frameshift with a predicted alternate stop codon after 14 amino acids. This alteration occurs at the 3' terminus of the SHANK3 gene, is not expected to trigger nonsense-mediated mRNA decay, and only impacts the last 11% of the protein. However, premature stop codons are typically deleterious in nature, the impacted region is critical for protein function, and a significant portion of the protein is affected (Ambry internal data). This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). This variant has been determined to be the result of a de novo mutation in one individual with features consistent with Phelan-McDermid syndrome (Kohlenberg, 2020). Based on the available evidence, this alteration is classified as pathogenic. |