Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000497975 | SCV000589332 | uncertain significance | not provided | 2017-06-16 | criteria provided, single submitter | clinical testing | A variant of uncertain significance has been identified in the GATM gene. The c.-1 G>A sequence change in the 5' untranslated region of GATM has not been published as a pathogenic variant, nor has it been reported as a benign variant to our knowledge. The c.-1 G>A variant is not observed in large population cohorts; however, limited data are available (Lek et al., 2016; 1000 Genomes Consortium et al., 2015; Exome Variant Server). This substitution occurs at a position in the Kozak sequence that is not conserved, and it is not expected to alter the ATG initiation codon. Additionally, other regulatory variants have not been reported in the GATM gene in association with AGAT deficiency (Stenson et al., 2014). However, in the absence of RNA/functional studies, the actual effect of this sequence change in this individual is unknown. Therefore, based on the currently available information, it is unclear whether this variant is a pathogenic variant or a rare benign variant. |
Ambry Genetics | RCV002318601 | SCV000850388 | uncertain significance | Inborn genetic diseases | 2024-01-17 | criteria provided, single submitter | clinical testing | The c.-1G>A variant is located in the 5' untranslated region (5’ UTR) of the GATM gene. This variant results from a G to A substitution 1 bases upstream from the first translated codon. This nucleotide position is not well conserved in available vertebrate species. Since supporting evidence is limited at this time, the clinical significance of this variant remains unclear. |
Fulgent Genetics, |
RCV002475983 | SCV002792513 | uncertain significance | Arginine:glycine amidinotransferase deficiency; Fanconi renotubular syndrome 1 | 2022-04-28 | criteria provided, single submitter | clinical testing |