Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003448335 | SCV004176255 | likely pathogenic | Hereditary thrombocytopenia and hematologic cancer predisposition syndrome | 2023-12-09 | reviewed by expert panel | curation | NM_001754.5(RUNX1):c.593A>C (p.Asp198Ala) is a missense variant. This variant is completely absent from all population databases with at least 20x coverage for RUNX1 in gnomAD v2.1.1 and v3.1.2 (PM2_supporting). This variant affects an amino acid residue within the RHD domain that is defined as a mutational hotspot by the ClinGen MM-VCEP (PM1). The REVEL score is ≥ 0.88 (0.962) (PP3). Two other missense variants (c.593A>T, p.Asp198Val, ClinVar Variation ID 627342 and c.592G>T (p.Asp198Tyr), CA410207975) in the same codon has been classified as likely pathogenic for Hereditary thrombocytopenia and hematologic cancer predisposition syndrome by the ClinGen MMVCEP (PM5_Supporting). This variant has been reported in a proband with AML, meeting RUNX1-phenotypic criteria (PS4_supporting, internal data from PreventionGenetics). In summary, the clinical significance of this variant is likely pathogenic. ACMG/AMP criteria applied, as specified by the Myeloid Malignancy Variant Curation Expert Panel for RUNX1: PM1, PM2_supporting, PP3, PM5_supporting, PS4_supporting. |
Prevention |
RCV000680424 | SCV000807795 | likely pathogenic | not provided | 2021-09-21 | criteria provided, single submitter | clinical testing |