Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001215896 | SCV004176275 | pathogenic | Hereditary thrombocytopenia and hematological cancer predisposition syndrome associated with RUNX1 | 2023-12-09 | reviewed by expert panel | curation | NM_001754.5(RUNX1):c.967+2_967+5del is a noncoding variant. This variant was found to co-segregate with disease in multiple affected family members, with seven or more (8) meioses observed in one family/across 1 family (PP1_Strong; PMID: 28240786). Skips exon 8 with in frame del270- 323 and D269A deletion in TAD(PVS1_strong). This variant has been reported in two or three probands (X) meeting at least one of the RUNX1-phenotypic criteria (PS4_Moderate; PMID: 28240786, doi: 10.1093/ajcp/aqz121.026) (PS4_moderate). This variant is completely absent from all population databases with at least 20x coverage for RUNX1 (PM2_supporting). In summary, this variant meets criteria to be classified as pathogenic. ACMG/AMP criteria applied, as specified by the Myeloid Malignancy Variant Curation Expert Panel for RUNX1: PP1_strong, PVS1_strong, PS4_moderate, PM2_supporting |
Labcorp Genetics |
RCV001215896 | SCV001387664 | pathogenic | Hereditary thrombocytopenia and hematological cancer predisposition syndrome associated with RUNX1 | 2019-09-15 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Donor and acceptor splice site variants typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in RUNX1 are known to be pathogenic (PMID: 18723428, 24100448). Experimental studies have shown that this variant disrupts mRNA splicing (PMID: 28240786). This variant has been observed in a family affected with thrombocytopenia and acute myeloid leukemia (PMID: 28240786). This variant is not present in population databases (ExAC no frequency). This sequence change affects a donor splice site in intron 8 of the RUNX1 gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. |
Zotz- |
RCV001215896 | SCV004101064 | pathogenic | Hereditary thrombocytopenia and hematological cancer predisposition syndrome associated with RUNX1 | 2023-11-02 | no assertion criteria provided | clinical testing |