Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV004692766 | SCV005196561 | likely pathogenic | Hereditary thrombocytopenia and hematologic cancer predisposition syndrome | 2024-08-01 | reviewed by expert panel | curation | NM_001754.5(RUNX1):c.999dup (p.Arg334fs) is a frameshift variant in exon 8 which is predicted to not undergo nonsense-mediated mRNA decay (PVS1_strong). It is downstream of c.98 (PM5_supporting). This variant is completely absent from all population databases with at least 20x coverage for RUNX1 (PM2_supporting). In summary, this variant meets criteria to be classified as likely pathogenic. ACMG/AMP criteria applied, as specified by the Myeloid Malignancy Variant Curation Expert Panel for RUNX1: PVS1_strong, PM2_supporting, PM5_supporting. |
Genetic Services Laboratory, |
RCV001817928 | SCV002067411 | likely pathogenic | not provided | 2020-02-24 | criteria provided, single submitter | clinical testing | DNA sequence analysis of the RUNX1 gene demonstrated a 1 base pair duplication in exon 9, c.999dup. The c.999dup sequence change has not been described in population databases (gnomAD, ExAC). This sequence change is predicted to result in a frameshift leading to the formation of a premature stop codon 265 amino acids downstream of the duplication, p.Arg334Alafs*266. While this duplication has not previously been described in the literature, other frameshift duplications in the RUNX1 gene have been described in patients with RUNX1-related disorders (PMIDs: 19357396, 28181366). |