Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000079915 | SCV000111798 | uncertain significance | not provided | 2012-08-13 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000055866 | SCV005077376 | likely pathogenic | Carnitine palmitoyl transferase 1A deficiency | 2024-04-05 | criteria provided, single submitter | clinical testing | Variant summary: CPT1A c.367C>T (p.Arg123Cys) results in a non-conservative amino acid change in the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 8e-06 in 251302 control chromosomes (gnomAD). c.367C>T has been reported in the literature in a homozygous individual affected with Carnitine Palmitoyltransferase I Deficiency (Brown_2001). These data indicate that the variant may be associated with disease. This publication reports experimental evidence evaluating an impact on protein function. Fibroblasts from the patient had L-CPT I activity ~9% of control cells, while COS cells transfected with the variant showed ~72% of normal activity. The exogenously expressed variant protein had an aberrant molecular weight, suggesting that processing defects and degradation in vivo may explain this discrepancy. The following publication have been ascertained in the context of this evaluation (PMID: 11441142). ClinVar contains an entry for this variant (Variation ID: 65653). Based on the evidence outlined above, the variant was classified as likely pathogenic. |
Fulgent Genetics, |
RCV000055866 | SCV005630244 | likely pathogenic | Carnitine palmitoyl transferase 1A deficiency | 2024-04-10 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000055866 | SCV000086869 | not provided | Carnitine palmitoyl transferase 1A deficiency | no assertion provided | literature only |