Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Equipe Genetique des Anomalies du Developpement, |
RCV000755704 | SCV000883140 | uncertain significance | Dilated cardiomyopathy 1I | 2018-11-21 | criteria provided, single submitter | clinical testing | |
Revvity Omics, |
RCV001784366 | SCV002024044 | likely pathogenic | not provided | 2022-12-30 | criteria provided, single submitter | clinical testing | |
Ambry Genetics | RCV002406675 | SCV002714681 | uncertain significance | Cardiovascular phenotype | 2022-02-03 | criteria provided, single submitter | clinical testing | The p.R355* variant (also known as c.1063C>T), located in coding exon 6 of the DES gene, results from a C to T substitution at nucleotide position 1063. This changes the amino acid from an arginine to a stop codon within coding exon 6. This variant has been reported as a secondary finding in a whole exome sequencing cohort; however, clinical details were limited (Thauvin-Robinet C et al. Eur J Hum Genet, 2019 08;27:1197-1214). This alteration is expected to result in loss of function by premature protein truncation or nonsense-mediated mRNA decay. Although biallelic loss of function alterations in DES have been associated with autosomal recessive DES-related myopathy, haploinsufficiency for DES has not been clearly established as a mechanism of disease for autosomal dominant DES-related myopathy. Since supporting evidence is limited at this time, the clinical significance of this alteration remains unclear. |
Laboratory for Molecular Medicine, |
RCV004017725 | SCV004847600 | likely pathogenic | Desmin-related myofibrillar myopathy | 2019-02-08 | criteria provided, single submitter | clinical testing | The p.Arg355X variant in DES has not been previously reported in individuals with desmin-related myopathy but has been identified in 1/113718 European chromosomes by the Genome Aggregation Database (gnomAD, http://gnomad.broadinstitute.org). This nonsense variant leads to a premature termination codon at position 355, which is predicted to lead to a truncated or absent protein. Heterozygous loss of function of the DES gene is an established disease mechanism in desmin-related myopathy. In summary, although additional studies are required to fully establish its clinical significance, the p.Gln355X variant is likely pathogenic. ACMG/AMP Criteria applied: PVS1, PM2. |