Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV002265627 | SCV000197523 | likely pathogenic | Desmin-related myofibrillar myopathy | 2014-03-05 | criteria provided, single submitter | clinical testing | The 735+1G>C variant in DES has not been previously reported in individuals with cardiomyopathy or in large population studies. This variant occurs in the invar iant region (+/- 1,2) of the splice consensus sequence and is predicted to cause altered splicing leading to an abnormal or absent protein. Another variant at t his position (735+1G>A) has been reported in 2 individuals with desminopathy (Re ported as IVS3+1G>A: Gudkova 2013 and Shatunov et al., unpublished data, reviewe d by Goldfarb 2004) and identified by our laboratory as a de novo occurrence in 1 individual with desminopathy. In summary, the 735+1G>C variant is likely patho genic, though additional studies are required to fully establish its clinical si gnificance. |
Institute of Immunology and Genetics Kaiserslautern | RCV002265627 | SCV005093843 | pathogenic | Desmin-related myofibrillar myopathy | 2024-07-19 | criteria provided, single submitter | clinical testing | ACMG Criteria: PVS1, PM2, PP5; Variant was found in heterozygous state |