Total submissions: 8
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics Munich, |
RCV000017552 | SCV000680243 | pathogenic | Alexander disease | 2017-10-25 | criteria provided, single submitter | clinical testing | |
Ambry Genetics | RCV001267511 | SCV001445692 | pathogenic | Inborn genetic diseases | 2019-11-06 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000056848 | SCV002246484 | pathogenic | not provided | 2023-07-17 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with tryptophan, which is neutral and slightly polar, at codon 416 of the GFAP protein (p.Arg416Trp). This variant is present in population databases (rs121909717, gnomAD 0.01%). This missense change has been observed in individual(s) with Alexander disease (PMID: 11138011, 27814755). In at least one individual the variant was observed to be de novo. ClinVar contains an entry for this variant (Variation ID: 16169). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on GFAP protein function. Experimental studies have shown that this missense change affects GFAP function (PMID: 16826512). For these reasons, this variant has been classified as Pathogenic. |
Victorian Clinical Genetics Services, |
RCV000017552 | SCV002767965 | pathogenic | Alexander disease | 2021-05-06 | criteria provided, single submitter | clinical testing | Based on the classification scheme VCGS_Germline_v1.3.4, this variant is classified as Pathogenic. Following criteria are met: 0105 - The mechanism of disease for this gene is not clearly established. Fuctional studies have demonstrated both dominant negative and gain of function are possible mechanisms of disease, where the latter is the more widely accepted mechanism (OMIM, GeneReviews, PMID: 11138011, PMID: 30355500, PMID: 31484723). (I) 0107 - This gene is associated with autosomal dominant disease. (I) 0200 - Variant is predicted to result in a missense amino acid change from arginine to tryptophan. (I) 0251 - This variant is heterozygous. (I) 0302 - Variant is present in gnomAD (v2, v3) <0.001 for a dominant condition (1 heterozygote, 0 homozygotes). (SP) 0309 - An alternative amino acid change at the same position has been observed in gnomAD (v2) (21 heterozygotes, 0 homozygotes). (I) 0501 - Missense variant consistently predicted to be damaging by multiple in silico tools or highly conserved with a major amino acid change. (SP) 0600 - Variant is located in the annotated tail domain (PMID: 31611638). (I) 0801 - This variant has strong previous evidence of pathogenicity in unrelated individuals. This variant has been reported as pathogenic, and shown to be de novo in a patient with Alexander disease (ClinVar). It has also been reported in multiple other patients with infantile-, juvenile- and adult-onset Alexander disease, both familial and sporadic (PMID: 31611638, PMID: 18684770, PMID: 27814755). (SP) 1102 - Strong phenotype match for this individual. (SP) 1208 - Inheritance information for this variant is not currently available in this individual. (I) Legend: (SP) - Supporting pathogenic, (I) - Information, (SB) - Supporting benign |
Revvity Omics, |
RCV000017552 | SCV003818146 | pathogenic | Alexander disease | 2022-11-08 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000017552 | SCV000037824 | pathogenic | Alexander disease | 2006-08-01 | no assertion criteria provided | literature only | |
Epithelial Biology; Institute of Medical Biology, |
RCV000056848 | SCV000087961 | not provided | not provided | no assertion provided | not provided | ||
Gene |
RCV000017552 | SCV000223052 | not provided | Alexander disease | no assertion provided | literature only |