Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000056899 | SCV000321721 | pathogenic | not provided | 2020-04-30 | criteria provided, single submitter | clinical testing | Reported previously in the heterozygous state in at least one individual with Alexander syndrome (Brenner et al., 2001); Published functional studies demonstrate that mice harboring the R239H variant develop astrocyte pathology typical of Alexander disease (Hagerman et al., 2006; Sosunov et al., 2013; In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Not observed in large population cohorts (Lek et al., 2016); This variant is associated with the following publications: (PMID: 32180488, 11138011, 31484723, 28882119, 23432455, 24102621, 27966545, 27193225, 28359321, 27609520, 27798231, 27648269, 23616550, 17065456) |
Laboratory for Animal Genetics, |
RCV000017551 | SCV000607713 | pathogenic | Alexander disease | criteria provided, single submitter | in vivo | Similar disease in dogs: OMIA 001208-9615. Tetraplegia with spastic front limbs mimicking 'swimming puppy syndrome'; detection of GFAP containing Rosenthal fibers in astrocytes; Alexander's disease (AxD) in a Labrador retriever is caused by a heterozygous de novo dominant R240H GFAP mutation, orthologous to the human R239H hotspot mutation known to cause a severe AxD phenotype. | |
Ce |
RCV000056899 | SCV001746291 | pathogenic | not provided | 2021-09-01 | criteria provided, single submitter | clinical testing | |
DASA | RCV000017551 | SCV002526391 | pathogenic | Alexander disease | 2022-06-10 | criteria provided, single submitter | clinical testing | The c.716G>A;p.(Arg239His) missense change has been observed in affected individual(s) and ClinVar contains an entry for this variant (ClinVar ID: 16168; NBK1172; OMIM 137780.0001; PMID: 24427505; 17383133; 11567214; 21533827) - PS4.Well-established in vitro or in vivo functional studies supportive of a damaging effect on the gene or gene product (PMID: 17065456, 23432455 ) - PS3. This variant is not present in population databases:rs59565950, gnomAD; ABraOM no frequency - http://abraom.ib.usp.br/) - PM2. Missense variant in GFAP that has a low rate of benign missense variation and in which missense variants are a common mechanism of disease - PP2. Multiple lines of computational evidence support a deleterious effect on the gene or gene product - PP3. In summary, the currently available evidence indicates that the variant is Pathogenic |
OMIM | RCV000017551 | SCV000037823 | pathogenic | Alexander disease | 2005-03-01 | no assertion criteria provided | literature only | |
Epithelial Biology; Institute of Medical Biology, |
RCV000056899 | SCV000088012 | not provided | not provided | no assertion provided | not provided | ||
Gene |
RCV000017551 | SCV000222998 | not provided | Alexander disease | no assertion provided | literature only |