Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Kasturba Medical College, |
RCV000192137 | SCV002522652 | pathogenic | Alexander disease | criteria provided, single submitter | clinical testing | ||
Labcorp Genetics |
RCV000056901 | SCV003441992 | pathogenic | not provided | 2022-02-18 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This sequence change replaces arginine, which is basic and polar, with leucine, which is neutral and non-polar, at codon 239 of the GFAP protein (p.Arg239Leu). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individual(s) with Alexander disease (PMID: 17043438, 21041050, 34146839). In at least one individual the variant was observed to be de novo. ClinVar contains an entry for this variant (Variation ID: 66498). Algorithms developed to predict the effect of missense changes on protein structure and function (SIFT, PolyPhen-2, Align-GVGD) all suggest that this variant is likely to be disruptive. This variant disrupts the p.Arg239 amino acid residue in GFAP. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 11138011, 11587071). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. |
Epithelial Biology; Institute of Medical Biology, |
RCV000056901 | SCV000088014 | not provided | not provided | no assertion provided | not provided | ||
Gene |
RCV000192137 | SCV000223000 | not provided | Alexander disease | no assertion provided | literature only |