Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
UOS Fisiopatologia delle Anemie, |
RCV001352675 | SCV001433005 | pathogenic | Dehydrated hereditary stomatocytosis with or without pseudohyperkalemia and/or perinatal edema | 2020-08-28 | criteria provided, single submitter | clinical testing | The p. S314P variant in KCNN4 gene has been reported in 7 Italian patients from 2 unrelated families presenting mild hemolytic anemia. In vitro functional studies indicate that the S314P variant result in a gain of function mutation and in increase activation of the Gardos channel. The variant meets criteria to be classified as pathogenic based upon segregation studies, absence from controls, phenotypic and functional evidence |